A bicyclic 1-deoxygalactonojirimycin derivative as a novel pharmacological chaperone for GM1 gangliosidosis

Tomoko Takai, Katsumi Higaki, Matilde Aguilar-Moncayo, Teresa Mena-Barragán, Yuki Hirano, Kei Yura, Liang Yu, Haruaki Ninomiya, M. Isabel García-Moreno, Yasubumi Sakakibara, Kousaku Ohno, Eiji Nanba, Carmen Ortiz Mellet, José M. García Fernández, Yoshiyuki Suzuki

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